News
Researchers identified a unique protein signature in the blood of BMD and LGMD patients that may reflect disease progression.
Ifetroban improved heart function and reduced cardiac damage biomarkers in people with DMD in a Phase 2 clinical trial.
Summer can be rough for folks with muscular dystrophy, columnist Patrick Moeschen writes, but it can also bring adventures in appreciation.
The FDA has granted rare pediatric disease designation to PBGENE-DMD, an experimental gene-editing therapy for Duchenne ...
A recent dream leaves columnist Robin Stemple questioning how his disability progression due to FSHD affects his family and ...
The U.S. Food and Drug Administration is due to review data on deramiocel, a cell therapy up for approval for heart disease ...
Caregiving means that columnist Betty Vertin sometimes misses out on activities with her children who don't have DMD. Finding balance is key.
Columnist Betty Vertin is grateful to have the help of a hired caregiver, but it's also been a difficult adjustment, she says.
A recent concert in Singapore was all about finding harmony through the talents that unite us in life, writes columnist.
As a person living with DMD, these discussions struck a chord with me, because these types of issues profoundly affect my daily life. Healthcare interactions with patients with Duchenne often involve ...
A first death was announced in March and both occurred in people with DMD who were no longer able to walk. Following the deaths, the gene therapy’s developer Sarepta is overhauling its safety plans ...
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