The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...
Britain's National Health Service (NHS) will provide a cutting-edge gene therapy that aims to cure sickle cell disease, the ...
There will be a blood drive for sickle cell disease – the most common inherited blood disorder – this weekend in South Jersey ...
Charity organisation Sickle Cell Society has described the recommendation as a “major breakthrough” for sickle cell patients.
Around 1,700 people could be eligible for the one-time treatment, which is seen as a less risky alternative to a donor stem ...
NHS officials estimate that around 50 people a year will receive treatment now that it has been approved for use for certain ...
Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...
The Exa-cel gene therapy treatment is at the forefront of medical technology. It takes the person’s DNA and “edits” out the faulty sickle gene. It’s expensive, too. According to the manufacturer, ...
Read about exa-cel being rolled out on the NHS, providing a 'functional cure' for some patients with severe sickle cell ...
People in England to benefit from groundbreaking one-off gene therapy for severe sickle cell disease approved by NICE ...
Vertex Pharmaceuticals (VRTX) stock gains as England opts to reimburse its CRSPR (CRSP)-partnered gene therapy Casgevy to ...
The National Institute for Health and Care Excellence (NICE) has approved a one-off gene editing therapy to treat severe sickle cell disease (SCD) in people 12 years and over. In final draft guidance1 ...