Charity organisation Sickle Cell Society has described the recommendation as a “major breakthrough” for sickle cell patients.
Around 1,700 people could be eligible for the one-time treatment, which is seen as a less risky alternative to a donor stem ...
NHS officials estimate that around 50 people a year will receive treatment now that it has been approved for use for certain ...
The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...
Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...
The Exa-cel gene therapy treatment is at the forefront of medical technology. It takes the person’s DNA and “edits” out the faulty sickle gene. It’s expensive, too. According to the manufacturer, ...
Vertex Pharmaceuticals (Nasdaq: VRTX) announced today a reimbursement agreement with NHS England for eligible sickle cell ...
It is believed around 1,700 people could be eligible for the treatment, while the NHS estimates around 50 people a year will ...
Read about exa-cel being rolled out on the NHS, providing a 'functional cure' for some patients with severe sickle cell ...
The therapy involves taking stem cells out of a patient's bone marrow and editing a gene in the cells in a laboratory and ...
People in England to benefit from groundbreaking one-off gene therapy for severe sickle cell disease approved by NICE ...
NHS officials estimate around 50 people a year will receive treatment now it has been approved for use for certain patients with severe sickle cell disease. | ITV National News ...