Treatment with Spinraza (nusinersen) can help stabilize or improve motor function in adults with SMA, according to a new ...

A higher dose of Spinraza may be more effective than the currently approved dosing schedule for maintaining motor function in ...

treatment with OAV101 IT demonstrated stabilization of motor function over 52 weeks of follow-up in patients who had previously discontinued treatment with Spinraza (nusinersen) or Roche’s RHHBY ...

Additionally, in the phase IIIb STRENGTH study, treatment with OAV101 IT demonstrated stabilization of motor function over 52 weeks of follow-up in patients who had previously discontinued treatment ...

Novartis' OAV101 IT gene therapy showed positive results in Phase 3 trials for SMA, with data supporting its potential as a treatment option.

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Nusinersen significantly improved the motor function of the patients especially those with SMA type 1. “Our findings support early SMA screening and presymptomatic nusinersen administration to ...