REGENXBIO is a longtime player in the gene therapy space, but one that’s yet to bring its own therapy to market (in the early ...

This article explores the transformative potential and challenges of single cell omics in advancing our understanding of ...

A significant advancement in knowledge of the link between cognition and genetics has been made thanks to a study led by ...

The Exa-cel gene therapy treatment is at the forefront of medical technology. It takes the person’s DNA and “edits” out the faulty sickle gene. It’s expensive, too. According to the manufacturer, ...

D tumoroid models transform cancer research, accurately reflecting tumor biology and enabling effective drug testing and ...

Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...

WGAL reporter Gene Schenck, a US Army special forces veteran, was in the room when the shocking event happened. That evening, on WGAL, he shared his thoughts about what he had just witnessed. We've ...

When Disney Channel star Cameron Boyce died in 2019, his death was ruled a sudden unexpected death in epilepsy, otherwise ...

The National Institute for Health and Care Excellence (NICE) has approved a one-off gene editing therapy to treat severe sickle cell disease (SCD) in people 12 years and over. In final draft guidance1 ...

The UK’s Medicines and Healthcare Regulatory Agency (MHRA) approved Casgevy for sickle cell disease in 2023, followed by ...

It is believed around 1,700 people could be eligible for the treatment, while the NHS estimates around 50 people a year will ...

NHS officials estimate around 50 people a year will receive treatment now it has been approved for use for certain patients with severe sickle cell disease. | ITV National News ...