Huntington’s is an incurable and fatal genetic condition that progressively affects movement, balance and cognition. It is ...

An international team of researchers has taken an important step toward understanding how gene expression is controlled ...

Heart attacks are dangerous not just because of the initial event, but the long-term damage afterwards. Now scientists have ...

Researchers at the Broad Institute of MIT and Harvard have developed a gene-editing treatment for prion disease that extends ...

If corn was ever jealous of soybean's relationship with nitrogen-fixing bacteria, advancements in gene editing could one day ...

Our genes contain all the instructions our body needs to function, but their expression must be finely regulated to guarantee ...

Scientists have characterized the role of thousands of mutations in the BRCA2 cancer gene, findings that may help reassure ...

Common measurements for modified adeno-associated viruses (AAVs), a gene therapy delivery method, showed substantial ...

Patients with spinal muscular atrophy (SMA) type 2 showed improved motor ability when treated with intrathecal onasemnogene ...

It was 1992 when Gene Bowen hit rock bottom. As a tour manager for various rock bands in the ‘80s, his daily routine included ...

Since two gene therapies were approved for sickle cell disease in late 2023, only a handful of patients have started the ...