Since 2016, the FDA has approved three disease-modifying treatments for spinal muscular atrophy, with several ...

Chugai Pharma’s Evrysdi tablets 5mg receives Japanese approval to treat spinal muscular atrophy: Saturday, March 29, 2025, 11:00 Hrs [IST] Chugai Pharmaceutical Co., Ltd. announ ...

The startup is bringing into Phase 1 testing an experimental treatment it says could be more effective than marketed ...

Every month, for 70 minutes, community members with Parkinson’s disease or mobility issues meet at Krannert Center for the ...

Here is our list of the 11 Best Gene Therapy Stocks to Buy According to Analysts.

NASA astronauts could face 'life altering' changes to their bodies after being left stranded in space following a capsule ...

Butch Wilmore and Suni Williams suffer accelerated ageing, DNA damage and muscle loss after nine months aboard ISS ...

Sleep-disordered breathing occurs frequently in patients with spinal muscular atrophy and can be obstructive ... heart rate, body position, and abdominal and thoracic movements, which were ...

Spending months in space can have serious effects on the human body. NASA astronauts Butch Wilmore and Suni Williams recently ...

Alan Jackson, who dazzled at Opry 100 on Wednesday, has battled Charcot-Marie-Tooth disease for over a decade. Here's what to ...

The prolific country artist from Georgia has battled Charcot-Marie-Tooth disease for over a decade. Here's what to know about ...