Infants with SMA type 1 born since 2016 experience better functional outcomes and life expectancy with disease-modifying treatments.

For this SMA population there is an adequate treatment available and reimbursed. There are a lot of children treated with nusinersen in Belgium.” “There is no life-threatening situation in ...

with Pharmac funding the SMA disease modifying drugs nusinersen (Spinraza) and risdiplam (Evrysdi) respectively for people aged 18 years and under with pre-symptomatic SMA or symptomatic Type 1 ...

Fully funded treatment for SMA is available in Aotearoa New Zealand, with Pharmac funding the SMA disease modifying drugs nusinersen (Spinraza) and risdiplam (Evrysdi) respectively for people aged 18 ...

"To call us a bad friend? That, to me, is cruel," she said in an interview this week. "Lie about what you want, but don't say Canada has treated you poorly." As he ponders the imposition of crippling ...

Sage Therapeutics stock gained after it announced that its board of directors has rejected the unsolicited, non-binding proposal offer from biotech giant Biogen to acquire the remaining shares of ...

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Anthos Therapeutics is a clinical-stage biopharmaceutical company developing abelacimab, a potential first-in-class monoclonal antibody targeting the FXI inhibition pathwayAbelacimab is currently ...

Romeo and Juliet, well known for its tragic end between two lovers, was hit with a warning of “suicide” and “death”. Toby Young, the leader of Free Speech Union, hit out at the Bristol-based ...