The death of a 16-year-old boy evokes a lengthy battle to realize the benefit of cutting-edge gene therapy while also ...
After a patient taking the Duchenne muscular dystrophy gene therapy Elevydis died of liver injury ... Meanwhile, in November 2022, an FDA-sanctioned trial from the non-profit biotech Cure Rare Disease ...
No human infections have been identified. More information and details about the recall can be found at the FDA website.