New research has investigated the mechanism by which bivalency functions to poise genes for expression during cell differentiation, providing insight into a long-standing paradigm in the regulation of ...

Researchers uncover key mechanisms in gene regulation that may lead to better design of RNA-based medicines.

In this manuscript, we give an overview of historical aspects, as well as the current state of clinical trials and approved gene therapy products for commercialization in Brazil. Focusing on gene ...

Elevidys, a product developed by Sarepta Therapeutics Inc., scrupulously treats Duchenne muscular dystrophy DMD by delivering a micro-dystrophin gene to muscle cells, partially restoring ...

While DMD is currently incurable, hope lies in emerging treatments like ELEVIDYS (Delandistrogene Moxeparvovec Rokl), a gene therapy designed to help the muscles produce dystrophin. However ...

The 247Sports Transfer Portal includes players who have either announced their intent to enter or have officially entered the NCAA Transfer Portal. Under the college transfer policy, when a ...

The EMBARK study of Elevidys (delandistrogene moxeparvovec) was designed to support the expansion of the label for the recently approved gene therapy to include all ambulatory DMD patients ...

The TP53 gene is a gene that is mutated in many cancers. It is the most common gene mutation found in cancer cells. A tumor-suppressor gene, TP53 codes for a protein that inhibits the development and ...

We have reached the halfway point of the January transfer window and several sagas are coming to a head. Arsenal and Mikel Arteta are keen to add a new striker this month after Gabriel Jesus was ...

REGENXBIO's partnership with Nippon Shinyaku provides $110M upfront, ensuring a cash runway for gene therapy programs in MPS I & II, despite sacrificing some upside. REGENXBIO is rated a HOLD ...

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