This story was originally published on PharmaVoice. To receive daily news and insights, subscribe to our free daily PharmaVoice newsletter. Gene therapies have set a high bar for outcomes in ...

In most cases, people with type 2 diabetes can drink alcohol in moderate amounts. As you may well know, living with type 2 diabetes often means cutting out or cutting back on foods and beverages that ...

Duchenne muscular dystrophy (DMD) is a rare genetic disorder that is characterised by progressive muscle degeneration and weakness, and is caused by mutations in the dystrophin gene. Currently ...

INS1201 represents the first application of Insmed’s targeted AAV delivery platform in DMD. Credit: JHVEPhoto / Shutterstock. Duchenne muscular dystrophy (DMD) is a rare genetic disorder that is ...

adeno-associated virus (AAV)-based gene transfer therapy for intravenous infusion designed to address the underlying genetic cause of Duchenne muscular dystrophy – mutations or changes in the DMD gene ...

As a result, the majority of recombinant AAV (rAAV) gene therapy programs focus on these areas to address existing medical challenges, leveraging AAV’s tropism to enhance treatment efficacy and ...

About ELEVIDYS (delandistrogene moxeparvovec-rokl) ELEVIDYS (delandistrogene moxeparvovec-rokl) is a single-dose, adeno-associated virus (AAV ... or changes in the DMD gene that result in the ...

The CONNECT2-EDO51 phase 2 trial looks at PGN-EDO51, an investigational therapy for Duchenne muscular dystrophy (DMD), and is ... how various routes of adeno-associated virus (AAV) gene therapy ...

High-potency corticosteroids should not be used in intertriginous areas because they can quickly cause skin atrophy, striae, and even ulceration. Weaker corticosteroids should be used on the face ...