potency testing, and biodistribution. Enhanced AAV Critical Quality Attributes (CQAs) Streamline the Transition from AAV Vector Design to Comprehensive Gene Therapy QC Characterization Guangping ...

A new study in the peer-reviewed journal Human Gene Therapy describes a machine learning (ML) model that can be used as a ...

Two dose levels of a single-administration gene therapy were well-tolerated and led to functional improvements in ambulatory ...

The death of a young boy with Duchenne muscular dystrophy (DMD) who was treated with Pfizer’s experimental gene therapy in a phase 2 trial has prompted the company to pause dosing in another study.

VIENNA — Schistosoma haematobium can trigger cancer-related gene activity in the cervix, increasing the risk for cervical cancer, according to data presented at the ESCMID Global meeting. Healio ...