This story was originally published on PharmaVoice. To receive daily news and insights, subscribe to our free daily PharmaVoice newsletter. When Michelle Werner’s son Caffrey was diagnosed with ...

RFK Jr.'s Health Department shut down an advisory group that recommends how to test newborns for genetic disorders ...

The study highlights the importance of early and accurate diagnosis for distinct therapeutic approaches in DMD and BMD. Limitations include sample size discrepancies, potential steroid effects ...

Duchenne Muscular Dystrophy: diagnosis, clinical development and global researchMuscular dystrophy refers to a group of rare, genetic, progressive diseases that primarily affect the body’s muscles, ...

But the diagnosis ... (DMD), a muscle-wasting disorder primarily seen in male children. DMD first weakens the leg muscles. The first symptoms, mainly difficulty in walking, may show up in a child ...